Rare diseases
Investigational molecules
Locations
239 conditions with trials, the busiest first
755 trials across Europe, recruiting first
Study on the Safety and Effectiveness of Paltusotine for Patients with Acromegaly
BelgiumStudy of Fluconazole Treatment for Patients with Congenital Nephrogenic Diabetes Insipidus
DenmarkStudy on the Long-Term Safety and Effectiveness of Pegunigalsidase Alfa for Adults with Fabry Disease
BelgiumStudy of Weekly Infusions of JR-441 for Patients with Mucopolysaccharidosis Type IIIA
GermanyStudy on the Effectiveness and Safety of Vosoritide for Children with Hypochondroplasia
FranceStudy of Intrathecal Cebsulfase Alfa for Children with Late Infantile Metachromatic Leukodystrophy
BelgiumStudy on Long-Term Safety of INBRX-101 for Adults with Alpha-1 Antitrypsin Deficiency Emphysema
DenmarkStudy on the Effects of Paltusotine for Patients with Untreated Acromegaly
BulgariaStudy on Testosterone Undecanoate for Muscle Strength and Mass in Men with Obesity and Low Testosterone Undergoing Bariatric Surgery
DenmarkStudy on Treating Acute Gout Attacks with Prednisolone and Colchicine for Primary Care Patients
GermanyStudy Comparing Retatrutide and Tirzepatide for Weight Loss in Adults with Obesity
GermanyStudy on the Safety and Effects of VX-264 for Patients with Type 1 Diabetes
GermanyThe therapies tested most often in Metabolism and nutrition disorders trials.
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