Facioscapulohumeral muscular dystrophy
Not recruitingStudy on AOC 1020 for Adults with Facioscapulohumeral Muscular Dystrophy (FSHD)
Study on AOC 1020 for Adults with Facioscapulohumeral Muscular Dystrophy (FSHD)
- Disease:Facioscapulohumeral muscular dystrophy
- Substances:Humanised Igg1 Monoclonal Antibody Against Tfr1 Conjugated To Double Stranded Sirna Oligonucleotide Against Dux4 Mrna Via A Non-Cleavable Linker
Italy- Participants:18–64 years · 65+ years
- Substances:Humanised Igg1 Monoclonal Antibody Against Tfr1 Conjugated To Double Stranded Sirna Oligonucleotide Against Dux4 Mrna Via A Non-Cleavable Linker
- Sponsor:Avidity Biosciences Inc.













