Rare diseases
Investigational molecules
Locations
459 conditions with trials, the busiest first
1 397 trials across Europe, recruiting first
Study on the Effectiveness and Safety of Risdiplam for Children with Spinal Muscular Atrophy After Gene Therapy
GermanyStudy on the Safety and Effects of Acetylcysteine Amide for Patients Aged 12 and Over with Hereditary Cystatin C Amyloid Angiopathy
IcelandStudy on the Effects and Safety of Crovalimab for Adults and Adolescents with Atypical Hemolytic Uremic Syndrome (aHUS)
BelgiumStudy on the Effectiveness and Safety of GSK4527226 in Patients with Early Alzheimer's Disease
FinlandStudy on the Effects of Gemlapodect for Adults and Adolescents with Tourette Syndrome
BelgiumStudy Comparing Fluciclovine (18F) and Fluoroethyltyrosine F-18 PET Scans in Patients with New or Recurrent Brain Tumors and Brain Metastases
GermanyStudy of RO7269162 in people at risk for or with early-stage Alzheimer's Disease: Effects on brain amyloid buildup
DenmarkStudy on the Effects of AMX0035 (Phenylbutyrate and Ursodoxicoltaurine) in Patients with Progressive Supranuclear Palsy
AustriaStudy on the Safety and Effectiveness of 2-Hydroxyoleic Acid and Temozolomide with Radiotherapy for Patients with Newly Diagnosed Glioblastoma
FranceComparing Methotrexate and Tocilizumab for Treating Giant Cell Arteritis in Patients: A Study on Effectiveness and Safety
FranceStudy on the Long-Term Safety of Alpelisib for Patients with PIK3CA-Related Overgrowth Spectrum (PROS)
FranceStudy on Lasmiditan for Treating Migraine in Children Aged 6 to 17
BelgiumThe therapies tested most often in Nervous system disorders trials.
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