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Esteve Pharmaceuticals S.A.
Sponsor

Esteve Pharmaceuticals S.A.

Spain Passeig De La Zona Franca 109 Planta 4, 08038 Barcelona, Spain

About the sponsor

Esteve Pharmaceuticals S.A. is engaged in clinical research for mucopolysaccharidosis type IIIA, also known as Sanfilippo A syndrome, a rare inherited lysosomal storage disorder affecting the central nervous system and childhood development.

  • Mucopolysaccharidosis type IIIA
  • Sanfilippo A syndrome
  • Lysosomal storage disorder

The sponsor’s research interest is centered on neurological manifestations linked to this metabolic disease, with attention to conditions that involve progressive neurodegeneration and developmental impairment.

About Specializations

Esteve Pharmaceuticals S.A. runs clinical trials in conditions such as Mucopolysaccharidosis III, among others.

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Ongoing trials

Clinical trials registered by this sponsor – none is enrolling right now.

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1 clinical trial

Mucopolysaccharidosis III

Not recruiting

Study on the Safety and Initial Effects of AAV9-CAG-coh-SGSH in Children with Sanfilippo A Syndrome

InvestigationalNo placebo
Countries:SpainSpain
  • Participants:0–17 years
  • Substances:Adeno-Associated Viral Vector Serotype 9 Containing The Human Sulfamidase Gene
  • Sponsor:Esteve Pharmaceuticals S.A.

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