Not yet recruiting
Neuronal ceroid lipofuscinosis
Not yet recruitingFirst study of TTX-381 gene therapy safety in patients with eye problems caused by CLN2 disease (Neuronal Ceroid Lipofuscinosis Type 2)
InvestigationalNo placebo
First study of TTX-381 gene therapy safety in patients with eye problems caused by CLN2 disease (Neuronal Ceroid Lipofuscinosis Type 2)
InvestigationalNo placebo
- Disease:Neuronal ceroid lipofuscinosis
- Substances:TTX-381
Countries:
Germany
Germany- Participants:0–17 years
- Substances:TTX-381
- Sponsor:Tern Therapeutics LLC
