Glycogen storage disease type II
Not yet recruitingStudy on the Effects of Alglucosidase Alfa Enzyme Therapy in Children and Adults with Pompe Disease
Study on the Effects of Alglucosidase Alfa Enzyme Therapy in Children and Adults with Pompe Disease
- Disease:Glycogen storage disease type II
- Substances:Alglucosidase Alfa
The Netherlands- Participants:0–17 years · 18–64 years · 65+ years · Healthy volunteers
- Substances:Alglucosidase Alfa
- Sponsor:Erasmus Universitair Medisch Centrum Rotterdam (Erasmus MC)











